I was recently reminded of a pretty incredible story. In 2003, Beatrice “Bea” Rienhoff was born with contracted fingers, wide eyes, and a lack of muscle tone. It was clear by 6 months that she was not reaching developmental milestones on time and she was diagnosed with “failure to thrive”. Unfortunately, such a vague diagnosis has poor treatments and her parents were only given flax seed oil as a therapeutic. No prognosis was able to be made.
Can gene therapy fix any genetic defect?
Can gene therapy fix any genetic defect?
Can gene therapy fix any genetic defect?
I was recently reminded of a pretty incredible story. In 2003, Beatrice “Bea” Rienhoff was born with contracted fingers, wide eyes, and a lack of muscle tone. It was clear by 6 months that she was not reaching developmental milestones on time and she was diagnosed with “failure to thrive”. Unfortunately, such a vague diagnosis has poor treatments and her parents were only given flax seed oil as a therapeutic. No prognosis was able to be made.